Drug Information
Drug General Information | Top | |||
---|---|---|---|---|
Drug ID |
D8XHT1
|
|||
Drug Name |
RGX-111
|
|||
Drug Type |
Gene therapy
|
|||
Indication | Mucopolysaccharidosis [ICD-11: 5C56.3; ICD-9: 277.5] | Phase 1 | [1] | |
Company |
REGENXBIO
|
Target and Pathway | Top | |||
---|---|---|---|---|
Target(s) | Alpha-L-iduronidase (IDUA) | Target Info | Replacement | [2] |
References | Top | |||
---|---|---|---|---|
REF 1 | ClinicalTrials.gov (NCT03580083) RGX-111 Gene Therapy in Patients With MPS I. U.S. National Institutes of Health. | |||
REF 2 | Clinical pipeline report, company report or official report of REGENXBIO. |
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