Drug Information
Drug General Information | Top | |||
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Drug ID |
DZ97RW
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Drug Name |
4D-310
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Drug Type |
Gene therapy
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Indication | Fabry disease [ICD-11: 5C56.01; ICD-9: 272.7] | Phase 1/2 | [1] | |
Company |
4D Molecular Therapeutics
|
Target and Pathway | Top | |||
---|---|---|---|---|
Target(s) | Alpha-galactosidase A (GLA) | Target Info | . | [2] |
KEGG Pathway | Galactose metabolism | |||
Glycerolipid metabolism | ||||
Sphingolipid metabolism | ||||
Glycosphingolipid biosynthesis - globo series | ||||
Lysosome | ||||
Pathwhiz Pathway | Sphingolipid Metabolism | |||
Galactose Metabolism | ||||
Reactome | Glycosphingolipid metabolism | |||
WikiPathways | Sphingolipid metabolism |
References | Top | |||
---|---|---|---|---|
REF 1 | ClinicalTrials.gov (NCT04519749) An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry Disease. U.S.National Institutes of Health. | |||
REF 2 | Clinical pipeline report, company report or official report of 4D Molecular Therapeutics |
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