Drug Information
Drug General Information | Top | |||
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Drug ID |
DX71CK
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Drug Name |
QR1123
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Synonyms |
ION357
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Drug Type |
Antisense oligonucleotide
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Indication | Retinitis pigmentosa [ICD-11: 9B70; ICD-10: H35.5] | Phase 1/2 | [1] | |
Company |
ProQR Therapeutics Leiden, Netherlands Ionis Pharmaceuticals Carlsbad, CA
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Target and Pathway | Top | |||
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Target(s) | Rhodopsin P23H mutant messenger RNA (RHO P23H mRNA) | Target Info | . | [1] |
References | Top | |||
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REF 1 | ClinicalTrials.gov (NCT04123626) A Prospective First-In-Human Study to Evaluate the Safety and Tolerability of QR-1123 in Subjects With Autosomal Dominant Retinitis Pigmentosa (adRP) Due to the P23H Mutation in the RHO Gene. U.S.National Institutes of Health. |
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