Drug Information
| Drug General Information | Top | |||
|---|---|---|---|---|
| Drug ID |
DL7HD5
|
|||
| Drug Name |
RP-L102
|
|||
| Drug Type |
Gene therapy
|
|||
| Indication | Fanconi's anemia [ICD-11: 3A70.0] | Phase 2 | [1] | |
| Company |
Rocket Pharmaceuticals
|
|||
| Target and Pathway | Top | |||
|---|---|---|---|---|
| Target(s) | Fanconi anemia group A protein (FANCA) | Target Info | Replacement | [2] |
| References | Top | |||
|---|---|---|---|---|
| REF 1 | ClinicalTrials.gov (NCT04248439) Gene Therapy for Fanconi Anemia, Complementation Group A. U.S. National Institutes of Health. | |||
| REF 2 | Clinical pipeline report, company report or official report of Rocket Pharmaceuticals. | |||
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