Drug Information
| Drug General Information | Top | |||
|---|---|---|---|---|
| Drug ID |
D3W5TL
|
|||
| Drug Name |
ABO-102
|
|||
| Drug Type |
Gene therapy
|
|||
| Indication | Mucopolysaccharidosis [ICD-11: 5C56.3; ICD-9: 277.5] | Phase 1/2 | [1] | |
| Company |
Abeona Therapeutics
|
|||
| Target and Pathway | Top | |||
|---|---|---|---|---|
| Target(s) | N-sulphoglucosamine sulphohydrolase (SGSH) | Target Info | . | [2] |
| KEGG Pathway | Glycosaminoglycan degradation | |||
| Metabolic pathways | ||||
| Lysosome | ||||
| Reactome | HS-GAG degradation | |||
| WikiPathways | Glycosaminoglycan metabolism | |||
| References | Top | |||
|---|---|---|---|---|
| REF 1 | ClinicalTrials.gov (NCT04088734) Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease. U.S. National Institutes of Health. | |||
| REF 2 | Clinical pipeline report, company report or official report of Abeona Therapeutics. | |||
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